Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells
NCT00001234
·
clinicaltrials.gov ↗
PHASE1
Phase
COMPLETED
Status
120
Enrollment
NIH
Sponsor class
Conditions
Gaucher's Disease
Interventions
GENETIC:
human glucocerebrosidase cDNA
Sponsor
National Institute of Neurological Disorders and Stroke (NINDS)