# Gene Therapy for the Treatment of Fanconi's Anemia Type C

> **NCT00001399** · PHASE1 · COMPLETED · sponsor: **National Heart, Lung, and Blood Institute (NHLBI)** · enrollment: 9 (—)

## Conditions studied

- Fanconi's Anemia
- Pancytopenia

## Interventions

- **DRUG:** Transduced CD34+ Cells

## Key facts

- **NCT ID:** NCT00001399
- **Lead sponsor:** National Heart, Lung, and Blood Institute (NHLBI)
- **Sponsor class:** NIH
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 1993-12-03
- **Primary completion:** —
- **Final completion:** 2009-02-11
- **Target enrollment:** 9 (—)
- **Last updated:** 2017-07-02


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00001399

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00001399, "Gene Therapy for the Treatment of Fanconi's Anemia Type C". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT00001399. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*