Oral Pirfenidone for the Pulmonary Fibrosis of Hermansky-Pudlak Syndrome
Conditions
- Albinism
- Inborn Errors of Metabolism
- Oculocutaneous Albinism
- Platelet Storage Pool Deficiency
- Pulmonary Fibrosis
Interventions
- DRUG: Pirfenidone
- DRUG: Placebo
Sponsor
William Gahl, M.D.
Collaborators