Stem Cell Transplantation (SCT) for Genetic Diseases
Conditions
- Thrombocytopenia
- Metachromatic Leukodystrophy
- Fanconi's Anemia
- Thalassemia Major
- Pure Red-Cell Aplasia
- Inborn Errors of Metabolism
Interventions
- PROCEDURE: Stem Cell Transplantation
Sponsor
National Center for Research Resources (NCRR)
Collaborators