# Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase Deficiency

> **NCT00004386** · PHASE1 · TERMINATED · sponsor: **Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)**

## Conditions studied

- Ornithine Transcarbamylase Deficiency Disease

## Interventions

- **GENETIC:** recombinant adenovirus containing the ornithine transcarbamylase gene

## Key facts

- **NCT ID:** NCT00004386
- **Lead sponsor:** Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
- **Sponsor class:** NIH
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 1995-10
- **Primary completion:** —
- **Final completion:** —
- **Target enrollment:** — (—)
- **Last updated:** 2005-06-24

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00004386

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00004386, "Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase Deficiency". Retrieved via AI Analytics 2026-06-25 from https://api.ai-analytics.org/clinical/NCT00004386. Licensed CC0.

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