# Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome)

> **NCT00004454** · PHASE1,PHASE2 · COMPLETED · sponsor: **Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)** · enrollment: 2 (—)

## Conditions studied

- Mucopolysaccharidosis II

## Interventions

- **GENETIC:** lymphocyte gene therapy

## Key facts

- **NCT ID:** NCT00004454
- **Lead sponsor:** Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
- **Sponsor class:** NIH
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 1996-10
- **Primary completion:** —
- **Final completion:** —
- **Target enrollment:** 2 (—)
- **Last updated:** 2005-06-24

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00004454

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00004454, "Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome)". Retrieved via AI Analytics 2026-06-25 from https://api.ai-analytics.org/clinical/NCT00004454. Licensed CC0.

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