5-Azacytidine and Phenylbutyrate to Treat Severe Thalassemia
NCT00005934
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
24
Enrollment
NIH
Sponsor class
Conditions
Beta Thalassemia
Interventions
DRUG:
5-Azacytidine
Sponsor
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)