# Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid

> **NCT00007020** · PHASE3 · COMPLETED · sponsor: **Mirum Pharmaceuticals, Inc.** · enrollment: 85 (actual)

## Conditions studied

- Infantile Refsum's Disease
- Zellweger Syndrome
- Adrenoleukodystrophy
- Peroxisomal Disorders
- Cholestasis

## Interventions

- **DRUG:** Cholic Acids

## Key facts

- **NCT ID:** NCT00007020
- **Lead sponsor:** Mirum Pharmaceuticals, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 1992-01
- **Primary completion:** 2009-12
- **Final completion:** 2009-12
- **Target enrollment:** 85 (ACTUAL)
- **Last updated:** 2023-10-03

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00007020

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00007020, "Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid". Retrieved via AI Analytics 2026-06-16 from https://api.ai-analytics.org/clinical/NCT00007020. Licensed CC0.

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