# Alpha-Galactosidase A Replacement Therapy for Fabry Disease

> **NCT00048906** · PHASE2 · COMPLETED · sponsor: **National Institute of Neurological Disorders and Stroke (NINDS)** · enrollment: 3 (—)

## Conditions studied

- Fabry Disease

## Interventions

- **DRUG:** DRX005B

## Key facts

- **NCT ID:** NCT00048906
- **Lead sponsor:** National Institute of Neurological Disorders and Stroke (NINDS)
- **Sponsor class:** NIH
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2002-11
- **Primary completion:** —
- **Final completion:** 2003-11
- **Target enrollment:** 3 (—)
- **Last updated:** 2008-03-04


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00048906

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00048906, "Alpha-Galactosidase A Replacement Therapy for Fabry Disease". Retrieved via AI Analytics 2026-05-27 from https://api.ai-analytics.org/clinical/NCT00048906. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
