# Mucopolysaccharidosis I (MPS I) Registry

> **NCT00144794** · — · COMPLETED · sponsor: **Genzyme, a Sanofi Company** · enrollment: 1406 (actual)

## Conditions studied

- Mucopolysaccharidosis I (MPS I)

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT00144794
- **Lead sponsor:** Genzyme, a Sanofi Company
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2003-11-20
- **Primary completion:** 2024-12-31
- **Final completion:** 2024-12-31
- **Target enrollment:** 1406 (ACTUAL)
- **Last updated:** 2026-02-27


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00144794

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00144794, "Mucopolysaccharidosis I (MPS I) Registry". Retrieved via AI Analytics 2026-07-16 from https://api.ai-analytics.org/clinical/NCT00144794. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
