Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinosis

NCT00151216 · clinicaltrials.gov ↗

PHASE1

Phase

COMPLETED

Status

10

Enrollment

OTHER

Sponsor class

Conditions

Batten Disease
Late Infantile Neuronal Ceroid Lipofuscinosis

Interventions

BIOLOGICAL: AAV2CUhCLN2 (3x10^12 particle units)

Sponsor

Weill Medical College of Cornell University

Collaborators

[object Object]