Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I

NCT00215527 · clinicaltrials.gov ↗

PHASE1

Phase

TERMINATED

Status

4

Enrollment

INDIV

Sponsor class

Stopped Due to slow enrolment.

Conditions

Mucopolysaccharidosis I
Lysosomal Storage Diseases
Spinal Cord Compression

Interventions

DRUG: laronidase

Sponsor

Patricia I. Dickson, M.D.

Collaborators

[object Object]
[object Object]
[object Object]