# Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I

> **NCT00215527** · PHASE1 · TERMINATED · sponsor: **Patricia I. Dickson, M.D.** · enrollment: 4 (actual)

## Conditions studied

- Mucopolysaccharidosis I
- Lysosomal Storage Diseases
- Spinal Cord Compression

## Interventions

- **DRUG:** laronidase

## Key facts

- **NCT ID:** NCT00215527
- **Lead sponsor:** Patricia I. Dickson, M.D.
- **Sponsor class:** INDIV
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2005-11
- **Primary completion:** 2011-10
- **Final completion:** 2011-10
- **Target enrollment:** 4 (ACTUAL)
- **Why stopped:** Due to slow enrolment.
- **Last updated:** 2013-02-21

## Collaborators

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## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00215527

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00215527, "Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT00215527. Licensed CC0.

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