# Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy

> **NCT00227266** · PHASE2 · COMPLETED · sponsor: **University of Utah** · enrollment: 94 (actual)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

- **DRUG:** Valproic Acid and Levocarnitine
- **DRUG:** Placebo

## Key facts

- **NCT ID:** NCT00227266
- **Lead sponsor:** University of Utah
- **Sponsor class:** OTHER
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2005-09
- **Primary completion:** 2007-11
- **Final completion:** 2007-11
- **Target enrollment:** 94 (ACTUAL)
- **Last updated:** 2025-03-19

## Collaborators

- [object Object]
- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00227266

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00227266, "Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT00227266. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
