Treatment of the Cholesterol Defect in Smith-Lemli-Opitz Syndrome
NCT00272844
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
23
Enrollment
OTHER
Sponsor class
Conditions
Smith-Lemli-Opitz Syndrome
Interventions
DRUG:
crystalline cholesterol oil-based suspension
Sponsor
Boston Children's Hospital