Bone Marrow Cell Gene Transfer in Individuals With Fanconi Anemia
NCT00272857
·
clinicaltrials.gov ↗
PHASE1
Phase
COMPLETED
Status
3
Enrollment
OTHER
Sponsor class
Conditions
Fanconi Anemia
Interventions
GENETIC:
Retrovirus Construct
Sponsor
Boston Children's Hospital
Collaborators
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