GTA-Glyceryltriacetate for Canavan Disease
NCT00278707
·
clinicaltrials.gov ↗
PHASE1
Phase
UNKNOWN
Status
5
Enrollment
OTHER_GOV
Sponsor class
Conditions
Infantile Canavan Disease
Deficiency Disease, Aspartoacylase
Interventions
DRUG:
GTA: Glyceryltriacetate
Sponsor
Sheba Medical Center