# PTC124 for the Treatment of Cystic Fibrosis

> **NCT00351078** · PHASE2 · COMPLETED · sponsor: **PTC Therapeutics** · enrollment: 19 (actual)

## Conditions studied

- Cystic Fibrosis

## Interventions

- **DRUG:** PTC124

## Key facts

- **NCT ID:** NCT00351078
- **Lead sponsor:** PTC Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2006-12
- **Primary completion:** 2007-07
- **Final completion:** 2007-07
- **Target enrollment:** 19 (ACTUAL)
- **Last updated:** 2017-12-13


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00351078

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00351078, "PTC124 for the Treatment of Cystic Fibrosis". Retrieved via AI Analytics 2026-07-07 from https://api.ai-analytics.org/clinical/NCT00351078. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
