Safety and Efficacy Study of Phenoptin in Subjects With Hyperphenylalaninemia Due to BH4 Deficiency
NCT00355264
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
12
Enrollment
INDUSTRY
Sponsor class
Conditions
Tetrahydrobiopterin Deficiencies
Hyperphenylalaninemia, Non-Phenylketonuric
Interventions
DRUG:
Phenoptin
Sponsor
BioMarin Pharmaceutical