Pharmacokinetics and Tolerability of Zavesca® (Miglustat) In Patients With Juvenile GM2 Gangliosidosis

NCT00418847 · clinicaltrials.gov ↗

PHASE2

Phase

COMPLETED

Status

5

Enrollment

OTHER

Sponsor class

Conditions

Gangliosidoses GM2

Interventions

DRUG: miglustat

Sponsor

The Hospital for Sick Children

Collaborators

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