# Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy

> **NCT00428935** · PHASE1 · COMPLETED · sponsor: **Nationwide Children's Hospital** · enrollment: 6 (actual)

## Conditions studied

- Duchenne Muscular Dystrophy

## Interventions

- **BIOLOGICAL:** rAAV2.5-CMV-minidystrophin (d3990)

## Key facts

- **NCT ID:** NCT00428935
- **Lead sponsor:** Nationwide Children's Hospital
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2006-03
- **Primary completion:** 2009-03
- **Final completion:** 2010-07
- **Target enrollment:** 6 (ACTUAL)
- **Last updated:** 2013-02-05

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00428935

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00428935, "Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT00428935. Licensed CC0.

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