A Study of Gene-Activated® Human Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy in Gaucher Disease
NCT00430625
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
25
Enrollment
INDUSTRY
Sponsor class
Conditions
Gaucher Disease, Type 1
Interventions
BIOLOGICAL:
VPRIV ®,
Sponsor
Shire