A Study of AT2101 (Afegostat Tartrate) in Adult Patients With Type 1 Gaucher Disease Currently Receiving Enzyme Replacement Therapy
NCT00433147
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
30
Enrollment
INDUSTRY
Sponsor class
Conditions
Gaucher Disease, Type 1
Type 1 Gaucher Disease
Gaucher Disease
Interventions
DRUG:
Afegostat tartrate
Sponsor
Amicus Therapeutics