# A Study of AT2101 (Afegostat Tartrate) in Adult Patients With Type 1 Gaucher Disease Currently Receiving Enzyme Replacement Therapy

> **NCT00433147** · PHASE2 · COMPLETED · sponsor: **Amicus Therapeutics** · enrollment: 30 (actual)

## Conditions studied

- Gaucher Disease, Type 1
- Type 1 Gaucher Disease
- Gaucher Disease

## Interventions

- **DRUG:** Afegostat tartrate

## Key facts

- **NCT ID:** NCT00433147
- **Lead sponsor:** Amicus Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2007-03-23
- **Primary completion:** 2008-02-19
- **Final completion:** 2008-02-19
- **Target enrollment:** 30 (ACTUAL)
- **Last updated:** 2018-09-25


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00433147

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00433147, "A Study of AT2101 (Afegostat Tartrate) in Adult Patients With Type 1 Gaucher Disease Currently Receiving Enzyme Replacement Therapy". Retrieved via AI Analytics 2026-05-25 from https://api.ai-analytics.org/clinical/NCT00433147. Licensed CC0.

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