# Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I

> **NCT00439218** · PHASE1,PHASE2 · TERMINATED · sponsor: **Westat** · enrollment: 5 (actual)

## Conditions studied

- Spinal Muscular Atrophy Type I

## Interventions

- **DRUG:** sodium phenylbutyrate

## Key facts

- **NCT ID:** NCT00439218
- **Lead sponsor:** Westat
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2008-01
- **Primary completion:** 2009-05
- **Final completion:** 2009-05
- **Target enrollment:** 5 (ACTUAL)
- **Why stopped:** Extremely slow enrollment
- **Last updated:** 2010-11-09

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00439218

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00439218, "Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT00439218. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
