# Clinical Study of Spinal Muscular Atrophy

> **NCT00443066** · — · COMPLETED · sponsor: **Columbia University** · enrollment: 120 (actual)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT00443066
- **Lead sponsor:** Columbia University
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2005-05
- **Primary completion:** 2011-08-17
- **Final completion:** 2011-08-17
- **Target enrollment:** 120 (ACTUAL)
- **Last updated:** 2023-03-21

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00443066

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00443066, "Clinical Study of Spinal Muscular Atrophy". Retrieved via AI Analytics 2026-06-12 from https://api.ai-analytics.org/clinical/NCT00443066. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
