# A Study of Oral AT2101 (Afegostat Tartrate) in Treatment-naive Patients With Gaucher Disease

> **NCT00446550** · PHASE2 · COMPLETED · sponsor: **Amicus Therapeutics** · enrollment: 19 (actual)

## Conditions studied

- Gaucher Disease
- Type 1 Gaucher Disease
- Gaucher Disease, Type 1

## Interventions

- **DRUG:** afegostat tartrate

## Key facts

- **NCT ID:** NCT00446550
- **Lead sponsor:** Amicus Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2008-06-11
- **Primary completion:** 2009-08-20
- **Final completion:** 2009-08-20
- **Target enrollment:** 19 (ACTUAL)
- **Last updated:** 2018-08-15


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00446550

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00446550, "A Study of Oral AT2101 (Afegostat Tartrate) in Treatment-naive Patients With Gaucher Disease". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT00446550. Licensed CC0.

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