Efficacy and Safety Study of Genetically Targeted Enzyme Replacement Therapy for Advanced Heart Failure
Conditions
- Heart Failure, Congestive
- Dilated Cardiomyopathy
Interventions
- GENETIC: MYDICAR Phase 1 (Open-label, Serial Dose-Escalation Study)
- PROCEDURE: Placebo Infusion
- GENETIC: MYDICAR Phase 2 (Placebo-controlled, Randomized Study)
Sponsor
Celladon Corporation