# Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)

> **NCT00494195** · PHASE1 · COMPLETED · sponsor: **Nationwide Children's Hospital** · enrollment: 6 (actual)

## Conditions studied

- Muscular Dystrophies

## Interventions

- **GENETIC:** rAAV1.tMCK.human-alpha-sarcoglycan- First cohort
- **GENETIC:** Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Second cohort

## Key facts

- **NCT ID:** NCT00494195
- **Lead sponsor:** Nationwide Children's Hospital
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2008-03
- **Primary completion:** 2011-06
- **Final completion:** 2011-08
- **Target enrollment:** 6 (ACTUAL)
- **Last updated:** 2013-02-05

## Collaborators

- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00494195

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00494195, "Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)". Retrieved via AI Analytics 2026-06-30 from https://api.ai-analytics.org/clinical/NCT00494195. Licensed CC0.

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