# Miglustat in Niemann-Pick Type C Disease

> **NCT00517153** · PHASE2 · COMPLETED · sponsor: **Actelion** · enrollment: 29 (actual)

## Conditions studied

- Niemann-Pick Type C Disease

## Interventions

- **DRUG:** miglustat

## Key facts

- **NCT ID:** NCT00517153
- **Lead sponsor:** Actelion
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2002-01
- **Primary completion:** 2006-09
- **Final completion:** 2008-01
- **Target enrollment:** 29 (ACTUAL)
- **Last updated:** 2025-02-04


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00517153

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00517153, "Miglustat in Niemann-Pick Type C Disease". Retrieved via AI Analytics 2026-05-25 from https://api.ai-analytics.org/clinical/NCT00517153. Licensed CC0.

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