# A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients

> **NCT00568802** · PHASE1,PHASE2 · COMPLETED · sponsor: **Stanford University** · enrollment: 27 (actual)

## Conditions studied

- Muscular Atrophy, Spinal

## Interventions

- **DRUG:** Hydroxyurea
- **DRUG:** Placebo to match hydroxyurea

## Key facts

- **NCT ID:** NCT00568802
- **Lead sponsor:** Stanford University
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2004-01
- **Primary completion:** 2010-03
- **Final completion:** 2010-03
- **Target enrollment:** 27 (ACTUAL)
- **Last updated:** 2019-10-02


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00568802

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00568802, "A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT00568802. Licensed CC0.

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