Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
NCT00592553
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
174
Enrollment
INDUSTRY
Sponsor class
Conditions
Duchenne Muscular Dystrophy
Becker Muscular Dystrophy
Interventions
DRUG:
Ataluren
DRUG:
Placebo
Sponsor
PTC Therapeutics