Anaplerotic Therapy in Propionic Acidemia
NCT00645879
·
clinicaltrials.gov ↗
PHASE1
Phase
COMPLETED
Status
3
Enrollment
OTHER
Sponsor class
Conditions
Propionic Acidemia
Interventions
DRUG:
ornithine alpha ketoglutarate
DRUG:
glutamine
DRUG:
disodium citrate
Sponsor
Nicola Longo
Collaborators
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