# Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells

> **NCT00730314** · PHASE1,PHASE2 · COMPLETED · sponsor: **Children's Hospital Los Angeles** · enrollment: 25 (actual)

## Conditions studied

- Sickle Cell Disease
- Thalassemia
- Anemia
- Granuloma
- Wiskott-Aldrich Syndrome
- Chediak Higashi Syndrome
- Osteopetrosis
- Neutropenia
- Thrombocytopenia
- Hurler Disease
- Niemann-Pick Disease
- Fucosidosis

## Interventions

- **PROCEDURE:** Hematopoietic stem cell transplantation

## Key facts

- **NCT ID:** NCT00730314
- **Lead sponsor:** Children's Hospital Los Angeles
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2008-08
- **Primary completion:** 2015-08
- **Final completion:** 2015-08
- **Target enrollment:** 25 (ACTUAL)
- **Last updated:** 2016-06-23


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00730314

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00730314, "Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT00730314. Licensed CC0.

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