# Reduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant Disorders

> **NCT00744692** · PHASE1 · COMPLETED · sponsor: **Duke University** · enrollment: 22 (actual)

## Conditions studied

- Non Malignant Disorders
- Immunodeficiencies
- Congenital Marrow Failures
- Hemoglobinopathies
- Inborn Errors of Metabolism
- Sickle Cell
- Thalassemia
- Lysosomal Storage Disease

## Interventions

- **BIOLOGICAL:** Unrelated Umbilical Cord Blood Transplant
- **DRUG:** Reduced Intensity Conditioning

## Key facts

- **NCT ID:** NCT00744692
- **Lead sponsor:** Duke University
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2008-10
- **Primary completion:** 2012-12
- **Final completion:** 2014-04
- **Target enrollment:** 22 (ACTUAL)
- **Last updated:** 2014-08-13


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00744692

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00744692, "Reduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant Disorders". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT00744692. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
