# Extension Study of Long-term Safety and Efficacy of Myozyme for a Single Patient With Pompe Disease Who Were Previously Enrolled in Genzyme Sponsored ERT Studies.

> **NCT00765414** · PHASE2 · COMPLETED · sponsor: **Genzyme, a Sanofi Company** · enrollment: 1 (actual)

## Conditions studied

- Pompe Disease Late-Onset
- Glycogen Storage Disease Type II GSD II

## Interventions

- **BIOLOGICAL:** Myozyme

## Key facts

- **NCT ID:** NCT00765414
- **Lead sponsor:** Genzyme, a Sanofi Company
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2003-04
- **Primary completion:** 2006-04
- **Final completion:** 2006-08
- **Target enrollment:** 1 (ACTUAL)
- **Last updated:** 2014-02-05


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00765414

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00765414, "Extension Study of Long-term Safety and Efficacy of Myozyme for a Single Patient With Pompe Disease Who Were Previously Enrolled in Genzyme Sponsored ERT Studies.". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT00765414. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*