# Treatment of Dysphagia in Oculopharyngeal Muscular Dystrophy by Autologous Transplantation of Myoblasts

> **NCT00773227** · PHASE2 · COMPLETED · sponsor: **Assistance Publique - Hôpitaux de Paris** · enrollment: 30 (actual)

## Conditions studied

- Muscular Dystrophy, Oculopharyngeal

## Interventions

- **PROCEDURE:** Autologous myoblasts transplantation and myotomy

## Key facts

- **NCT ID:** NCT00773227
- **Lead sponsor:** Assistance Publique - Hôpitaux de Paris
- **Sponsor class:** OTHER
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2004-04
- **Primary completion:** 2015-07
- **Final completion:** 2015-10
- **Target enrollment:** 30 (ACTUAL)
- **Last updated:** 2015-11-20

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00773227

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00773227, "Treatment of Dysphagia in Oculopharyngeal Muscular Dystrophy by Autologous Transplantation of Myoblasts". Retrieved via AI Analytics 2026-06-09 from https://api.ai-analytics.org/clinical/NCT00773227. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
