PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry
NCT00778206
·
clinicaltrials.gov ↗
COMPLETED
Status
1887
Enrollment
INDUSTRY
Sponsor class
Conditions
Phenylketonuria
Hyperphenylalaninaemia
Interventions
DRUG:
Kuvan
Sponsor
BioMarin Pharmaceutical