# PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry

> **NCT00778206** · — · COMPLETED · sponsor: **BioMarin Pharmaceutical** · enrollment: 1887 (actual)

## Conditions studied

- Phenylketonuria
- Hyperphenylalaninaemia

## Interventions

- **DRUG:** Kuvan

## Key facts

- **NCT ID:** NCT00778206
- **Lead sponsor:** BioMarin Pharmaceutical
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2008-09
- **Primary completion:** 2021-01-29
- **Final completion:** 2021-01-29
- **Target enrollment:** 1887 (ACTUAL)
- **Last updated:** 2022-10-12


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00778206

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00778206, "PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry". Retrieved via AI Analytics 2026-08-11 from https://api.ai-analytics.org/clinical/NCT00778206. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*