# Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I

> **NCT00786968** · PHASE1 · TERMINATED · sponsor: **Patricia I. Dickson, M.D.** · enrollment: 3 (actual)

## Conditions studied

- Spinal Cord Compression
- Mucopolysaccharidosis I
- Hurler-Scheie Syndrome
- Scheie Syndrome
- Lysosomal Storage Disease

## Interventions

- **DRUG:** laronidase

## Key facts

- **NCT ID:** NCT00786968
- **Lead sponsor:** Patricia I. Dickson, M.D.
- **Sponsor class:** INDIV
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2008-01
- **Primary completion:** 2011-10
- **Final completion:** 2011-10
- **Target enrollment:** 3 (ACTUAL)
- **Why stopped:** Due to slow enrolment.
- **Last updated:** 2013-02-21

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00786968

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00786968, "Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I". Retrieved via AI Analytics 2026-09-22 from https://api.ai-analytics.org/clinical/NCT00786968. Licensed CC0.

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