# A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)

> **NCT00787995** · — · TERMINATED · sponsor: **BioMarin Pharmaceutical** · enrollment: 353 (actual)

## Conditions studied

- MPS IV A
- Mucopolysaccharidosis IVA
- Morquio A Syndrome

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT00787995
- **Lead sponsor:** BioMarin Pharmaceutical
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** TERMINATED
- **Start date:** 2008-10
- **Primary completion:** 2014-07
- **Final completion:** 2014-07
- **Target enrollment:** 353 (ACTUAL)
- **Last updated:** 2014-12-08


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT00787995

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT00787995, "A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)". Retrieved via AI Analytics 2026-06-24 from https://api.ai-analytics.org/clinical/NCT00787995. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
