A Long-Term Extension Study of AT2101 (Afegostat Tartrate) in Type 1 Gaucher Patients
NCT00813865
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
8
Enrollment
INDUSTRY
Sponsor class
Conditions
Gaucher Disease
Type 1 Gaucher Disease
Gaucher Disease, Type 1
Interventions
DRUG:
afegostat tartrate
Sponsor
Amicus Therapeutics