Efficacy and Safety of Human Lipoprotein Lipase (LPL)[S447X] Expressed by an Adeno-Associated Viral Vector in LPL-deficient Subjects

NCT00891306 · clinicaltrials.gov ↗

PHASE2,PHASE3

Phase

COMPLETED

Status

5

Enrollment

INDUSTRY

Sponsor class

Conditions

Familial Lipoprotein Lipase Deficiency

Interventions

GENETIC: Alipogene Tiparvovec (AMT-011), Human LPL [S447X]
DRUG: mycophenolate mofetil
DRUG: cyclosporine
DRUG: methylprednisolone

Sponsor

Amsterdam Molecular Therapeutics

Collaborators

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