Gene Therapy for X-linked Chronic Granulomatous Disease (CGD) in Children
NCT00927134
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
2
Enrollment
OTHER
Sponsor class
Conditions
Chronic Granulomatous Disease
Interventions
GENETIC:
retroviral SF71-gp91phox transduced CD34+ cells
Sponsor
University of Zurich
Collaborators
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