# Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases

> **NCT01003912** · PHASE1 · WITHDRAWN · sponsor: **Joanne Kurtzberg, MD**

## Conditions studied

- Lysosomal Storage Diseases
- Inborn Errors of Metabolism

## Interventions

- **BIOLOGICAL:** ALD-601

## Key facts

- **NCT ID:** NCT01003912
- **Lead sponsor:** Joanne Kurtzberg, MD
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** WITHDRAWN
- **Start date:** 2009-10
- **Primary completion:** 2017-03
- **Final completion:** 2017-03
- **Target enrollment:** 0 (ACTUAL)
- **Why stopped:** Patients were consented to screening but none were enrolled and proceeded with transplant.
- **Last updated:** 2017-06-29

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01003912

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01003912, "Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases". Retrieved via AI Analytics 2026-06-25 from https://api.ai-analytics.org/clinical/NCT01003912. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*