# Pilot Lenalidomide in Adult Diamond-Blackfan Anemia Patients w/ RBC Transfusion-Dependent Anemia

> **NCT01034592** · PHASE1 · TERMINATED · sponsor: **Jason Robert Gotlib** · enrollment: 2 (actual)

## Conditions studied

- Anemia
- Leukemia
- Acute Myeloid Leukemia (AML)
- Myelodysplastic Syndromes (MDS)

## Interventions

- **DRUG:** Lenalidomide

## Key facts

- **NCT ID:** NCT01034592
- **Lead sponsor:** Jason Robert Gotlib
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2009-11
- **Primary completion:** 2012-10
- **Final completion:** 2012-12
- **Target enrollment:** 2 (ACTUAL)
- **Why stopped:** Poor accrual related to rarity of Diamond-Blackfan anemia (DBA)
- **Last updated:** 2017-08-02

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01034592

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01034592, "Pilot Lenalidomide in Adult Diamond-Blackfan Anemia Patients w/ RBC Transfusion-Dependent Anemia". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT01034592. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
