Safety and Efficacy in LPL-Deficient Subjects of AMT-011, an Adeno-Associated Viral Vector Expressing Human Lipoprotein Lipase [S447X]

NCT01109498 · clinicaltrials.gov ↗

PHASE2,PHASE3

Phase

UNKNOWN

Status

14

Enrollment

INDUSTRY

Sponsor class

Conditions

Familial Lipoprotein Lipase Deficiency

Interventions

GENETIC: Alipogene Tiparvovec (AMT-011), Human LPL [S447X]
DRUG: Mycophenolate mofetil
GENETIC: Alipogene Tiparvovec (AMT-011), Human LPL [S447X]
DRUG: cyclosporine

Sponsor

Amsterdam Molecular Therapeutics

Collaborators

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