Pilot Study of Reduced-Intensity Hematopoietic Stem Cell Transplant of DOCK8 Deficiency

NCT01176006 · clinicaltrials.gov ↗

PHASE2

Phase

ACTIVE_NOT_RECRUITING

Status

70

Enrollment

NIH

Sponsor class

Conditions

DOCK8 Deficiency

Interventions

PROCEDURE: Reduced-intensity hematopoietic stem cell
DRUG: Fludarabine(Fludara, Berlex Laboratories)
DRUG: Cyclophosphamide(CTX, Cytoxan)
PROCEDURE: Total Body Irradiation (TBI)
DRUG: Busulfan (Busulfex)
PROCEDURE: Donor peripheral blood stem cell mobiliation and collection
PROCEDURE: Bone Marrow Harvest Procedure

Sponsor

National Cancer Institute (NCI)