# Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis

> **NCT01238328** · PHASE2,PHASE3 · UNKNOWN · sponsor: **Tehran University of Medical Sciences** · enrollment: 10 (estimated)

## Conditions studied

- Mucopolysaccharidosis

## Interventions

- **DRUG:** Conditioning regimen
- **DRUG:** Graft-versus-host disease (GVHD) prophylaxis
- **PROCEDURE:** Stem Cell Transplantation

## Key facts

- **NCT ID:** NCT01238328
- **Lead sponsor:** Tehran University of Medical Sciences
- **Sponsor class:** OTHER
- **Phase:** PHASE2,PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** UNKNOWN
- **Start date:** 2009-09
- **Primary completion:** 2012-09
- **Final completion:** 2012-12
- **Target enrollment:** 10 (ESTIMATED)
- **Last updated:** 2012-06-04


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01238328

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01238328, "Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT01238328. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
