# Gene Therapy ADA Deficiency

> **NCT01279720** · PHASE1,PHASE2 · COMPLETED · sponsor: **Great Ormond Street Hospital for Children NHS Foundation Trust** · enrollment: 8 (actual)

## Conditions studied

- Adenosine Deaminase Deficiency

## Interventions

- **BIOLOGICAL:** Intravenous infusion of transduced cells

## Key facts

- **NCT ID:** NCT01279720
- **Lead sponsor:** Great Ormond Street Hospital for Children NHS Foundation Trust
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2003-10
- **Primary completion:** 2013-11
- **Final completion:** 2013-11
- **Target enrollment:** 8 (ACTUAL)
- **Last updated:** 2015-09-14


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT01279720

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT01279720, "Gene Therapy ADA Deficiency". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT01279720. Licensed CC0.

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